Doctors Use CRISPR Technique for the First Time to Treat Genetic Disorder

Doctors in the United States are using the CRISPR technique for the first time to treat Sickle Cell disease. The doctors are modifying the patients’ own bone marrow with CRISPR to get the marrow to produce a protein which is only made a short time following birth. The belief is the protein created will combat sickle cell. 

Novel nanoparticles deliver CRISPR gene editing tools into the cell with much higher efficiency

Researchers developed a biodegradable synthetic lipid nanoparticle (which more easily penetrates the cell) to deliver CRISPR/Cas9. The nanoparticles encapsulate messenger RNA (mRNA) encoding Cas9. and once the contents of the nanoparticles are released the cell’s protein-making machinery creates Cas9 from the mRNA template.